We have a diverse pipeline designed to make a meaningful difference for patients
TransCon Therapies in Development
Our pipeline of TransCon therapies is driven by the flexibility of this innovative drug development platform and our aim to improve patients’ lives. Today, Ascendis and its partners have multiple prodrug therapies in development. Each product candidate is unique and designed to be a best-in-class therapy.
Endocrinology Rare Diseases
Ascendis Programs |
Clinical Trial |
Status |
Location |
|---|
TransCon hGH
|
Turner syndrome (children aged 1–10)
|
United States
|
Phase 2
|
New InsiGHTS Trial
NCT05690386 |
|
Multi-Indication (children aged 2–17)
Turner syndrome, Idiopathic Short Stature (ISS), SHOX Deficiency, and Small for Gestational Age (SGA) |
Multinational
|
Phase 3
|
HighLiGHts Trial
NCT07221851 |
TransCon CNP
|
Achondroplasia (infants aged 0–<2)
|
Multinational
|
Pivotal Phase 2
|
reACHin Trial
NCT06079398 |
|
Achondroplasia (children aged 2–11)
|
Multinational
|
Pivotal Phase 2
|
ApproaCH Trial
NCT05598320 |
|
Achondroplasia (adolescents aged 12–18)
|
Multinational
|
Pivotal Phase 2b
|
teACH Trial
NCT06732895 |
|
Achondroplasia (children & adolescents)
|
Multinational
|
Open Label Extension Trial
|
AttaCH Trial
NCT05929807 |
TransCon CNP + TransCon hGH
|
Achondroplasia (children aged 2–11)
|
Multinational
|
Phase 2
|
COACH Trial
NCT06433557 |
TransCon PTH
|
Adult Hypoparathyroidism (dosing expansion)
|
United States
|
Phase 3
|
PaTHway60 Trial
NCT07081997 |
Partner Programs |
Clinical Trial |
Status |
Location |
|---|
TransCon hGH
|
Pediatric GHD
|
China
|
Phase 3
|
VISEN Pharmaceuticals
|
|
Pediatric GHD
|
Japan
|
Phase 3
|
Teijin Pharma
Japan riGHt Trial |
TransCon CNP
|
Achondroplasia
|
China
|
Phase 2
|
VISEN Pharmaceuticals
ACcomplisH China Trial |
|
Achondroplasia
|
Japan
|
Phase 3
|
Teijin Pharma
Japan ApproaCH Trial |
TransCon PTH
|
Adult Hypoparathyroidism
|
China
|
Phase 3
|
VISEN Pharmaceuticals
PaTHway China Trial |
Oncology
Ascendis Programs |
Clinical Trial |
Status |
Location |
|---|
TransCon IL-2 β/γ (Systemic)
|
Various tumor types
|
Multinational
|
Phase 2
|
IL-Believe Trial
NCT05081609 |



